PublicationsStrategies to improve the design of gapmer antisense oligonucleotide on allele-specific silencing
Seminar SeriesThe Most Important Aspects of the Guidelines for N=1 Exon Skipping Design and in vitro Development
Illustrated ExamplesConsensus Guidelines for the Design and In Vitro Preclinical Efficacy Testing N=1 Exon Skipping ASOs
Illustrated ExamplesNonclinical Testing Draft GuidanceNonclinical Testing of Individualized Antisense Oligonucleotide Drug Products for Severely Debilitating or Life-Threatening Diseases...
