Milasen

• ​Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease, Oct 2019

• Drug Regulation in the Era of Individualized Therapies, Oct 2019

News Coverage:

• Science

• STAT

• MIT Tech Review

Oligonucleotide Therapeutics Society

• ​​OTS Rare Disease N-of-1+ Briefing Document, Jan 2020

Afinersen

• Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide, Dec 2021

News Coverage:

• Nature Medicine

Jacifusen

• Antisense oligonucleotide silencing of FUS expression as a therapeutic approach in amyotrophic lateral sclerosis, Jan 2022

News Coverage:

• STAT

Atipeksen ​

News Coverage:

• MIT Tech Review

Valeriasen

News Coverage:

• Gene Treatment for Rare Epilepsy Causes Brain Side Effect in 2 Children