N=1 Collaborative

Today, individualized medicines are possible.

We are on a mission to make them safe and rapidly accessible to patients worldwide.

Scientist

We envision a future where individualized medicine centers around the world routinely offer patients customized treatments targeting their condition’s underlying

genetic cause.

Our Story

Our Story

What started as a race against time for one little girl has turned into a movement that could help solve the global health crisis of rare genetic diseases.

Our Work

Our Work

With an initial focus on antisense oligonucleotides (ASOs), we are challenging and establishing the critical steps in the development of individualized medicines.

Who We Are

Who We Are

We are a group of internationally acclaimed doctors, researchers, patients and companies from across the globe who are committed to expanding the field of individualized medicine.