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Pilot launched to support children with rare conditions to access personalised therapies
Genomics England November 22, 2023 New programme announced to develop a pathway for children with rare conditions to access therapies...
What We Owe Terry Horgan: Reflections from Providers, Family, and Scientists
October 12, 2023 I first saw Terry Horgan as a patient. I was filling in as the pediatric pulmonary specialist in the UMass-Duchenne...
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