PublicationsStrategies to improve the design of gapmer antisense oligonucleotide on allele-specific silencing
Seminar SeriesTransforming Patient Access to High-Cost, One-Time Treatments through Financial Engineering Innovation
Articles & PodcastsBuilding a Bridge Between Rare Disease Patients and the Technologies that Could Help Them
Articles & PodcastsCan AI build custom ‘n-of-1’ drugs faster? Maybe not yet, new case study suggests
