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Accelerated approval will be 'the norm' for gene therapies, FDA's Peter Marks says

Zachary Brennan (Endpoints News) February 27, 2027 The FDA will increasingly use accelerated approval for gene therapies aimed at rare...

Articles & Podcasts

Four Keys To Advancing Antisense Oligonucleotides For Personalized Medicine

Demaris Mills (Forbes) January 12, 2024 The 2023 Oligonucleotide Therapeutics Society meeting drew 800 attendees to Barcelona, a clear...

Connecting, Collaborating, Communicating, Challenges: Sharing experiences navigating family conversations in an n-of-1 investigational treatment setting

Patient Partners: Harnessing synergies to pursue ASOs as part of the AHC research portfolio

Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders

Illustrated Examples

N1C Patient Identification Workgroup: Compilation of Useful Tools

Parents of Pioneers: Real experiences in individualized medicines today

Articles & Podcasts

This lifesaving treatment was designed for one. Could it be the future of medical care?

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