Seminar SeriesPRAX-222 Therapy for a Child: Prenatal Onset SCN2A Developmental and Epileptic Encephalopathy in a Named Patient Setting
Illustrated ExamplesN1C Preclinical Workgroup: Valuable Tools for the Preclinical Stage of Developing Potential Therapeutics Click below for download
Seminar Series"Control of starting material quality for oligonucleotide therapeutics" and "To Synthesis and Beyond…Production of oligos for ‘N-of-1’ therapies"
Illustrated ExamplesCommunity Job OpeningsWelcome to our community job board where we curate relevant job openings to share with our community. If you have a job post to share, we...
Articles & PodcastsAccelerated approval will be 'the norm' for gene therapies, FDA's Peter Marks saysZachary Brennan (Endpoints News) February 27, 2027 The FDA will increasingly use accelerated approval for gene therapies aimed at rare...
Articles & PodcastsFour Keys To Advancing Antisense Oligonucleotides For Personalized MedicineDemaris Mills (Forbes) January 12, 2024 The 2023 Oligonucleotide Therapeutics Society meeting drew 800 attendees to Barcelona, a clear...
